Rett syndrome

Silhouette of Businessman Entering Lit Door Passage in Darkness
Biotech

Astellas turns down option to license Taysha gene therapy—again

The biotech plans to advance the gene therapy into late-stage development, with the launch of a pivotal trial slated for this quarter.
Gabrielle Masson Oct 17, 2025 10:50am
gene therapy AAV adeno-associated viruses

Neurogene details death in Rett syndrome gene therapy trial

May 16, 2025 3:00pm
Digitally generated DNA fragment on a dark background

Patient put in critical condition by Neurogene gene therapy dies

Nov 22, 2024 3:57am
Gene editing CRISPR gene therapy

Neurogene acts as gene therapy puts person in critical condition

Nov 18, 2024 8:33am
money funding financing bank

Acadia makes $100M profit from $150M pediatric voucher sale

Nov 6, 2024 9:36am
Toxoplasma gondii

A brain parasite has been turned into drug delivery system

Jul 29, 2024 2:55pm